Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma

Aim: To analyze antitumor efficacy of experimental cancer vaccine therapy combined with introduction of vitamin D3 (VD3) for treatment of Lewis lung carcinoma (3LL). Materials and Methods: Cancer vaccines composed from recombinant murine beta-defensin-2 (mBD-2) and 3LL cell lysate, or DNA, coding fo...

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Published in:Experimental Oncology
Date:2010
Main Authors: Zhuravel, E., Efanova, O., Shestakova, T., Glushko, N., Mezhuev, O., Soldatkina, M., Pogrebnoy, P.V.
Format: Article
Language:English
Published: Інститут експериментальної патології, онкології і радіобіології ім. Р.Є. Кавецького НАН України 2010
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Cite this:Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma / E. Zhuravel, O. Efanova, T. Shestakova, N. Glushko, O. Mezhuev, M. Soldatkina, P.V. Pogrebnoy // Experimental Oncology. — 2010. — Т. 32, № 1. — С. 33-39. — Бібліогр.: 37 назв. — англ.

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Digital Library of Periodicals of National Academy of Sciences of Ukraine
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spelling Zhuravel, E.
Efanova, O.
Shestakova, T.
Glushko, N.
Mezhuev, O.
Soldatkina, M.
Pogrebnoy, P.V.
2018-06-19T10:17:39Z
2018-06-19T10:17:39Z
2010
Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma / E. Zhuravel, O. Efanova, T. Shestakova, N. Glushko, O. Mezhuev, M. Soldatkina, P.V. Pogrebnoy // Experimental Oncology. — 2010. — Т. 32, № 1. — С. 33-39. — Бібліогр.: 37 назв. — англ.
1812-9269
https://nasplib.isofts.kiev.ua/handle/123456789/138597
Aim: To analyze antitumor efficacy of experimental cancer vaccine therapy combined with introduction of vitamin D3 (VD3) for treatment of Lewis lung carcinoma (3LL). Materials and Methods: Cancer vaccines composed from recombinant murine beta-defensin-2 (mBD-2) and 3LL cell lysate, or DNA, coding for mBD-2-Muc1 fusion construct cloned in pcDNA3+ vector, were prepared and used for intradermal vaccination. Experimental cancer vaccines introduced i. d. at therapeutic and prophylactic regimens to 3LLbearing C57Bl mice, were applied alone or in combination with VD3 (administered per os) and/or low-dose cyclophosphamide (CP, administered intraperitoneal). Efficacy of treatments was analyzed by primary tumor growth dynamics indexes and by metastasis rate in vaccinated animals. Results: As it has been shown, administration of the protein-based vaccine composed from mBD-2 and 3LL cell lysate in combination with VD3 and CP, but not in VD3 free setting, led to significant suppression of primary tumor growth (p < 0.005) and had significant antimetastatic effect. Introduction of VD3 with or without CP in the scheme of treatment with mBD-2-Muc1-DNA vaccine at therapeutic regimen has led to significant suppression of primary tumor (p < 0.05) and metastasis volumes (p < 0.005), while in the groups of animals treated with DNA-vaccine + VD3 with or without CP at prophylactic regimen, significant antimetastatic effect (p < 0.05) and elevation of average life-span (p < 0.05) have been registered. Conclusion: The results of this pilot study have shown promising clinical effects of VD3 administration in combination with cancer vaccinotherapy in vivo.
The work was supported by NASU grants 0107U005545, the Program “Newest Medico- Biological Problems and Environment”, Part 2. “Biologically Active Compounds for Human Health” (Ukraine), and U002243 “Fundamental Problems of Genomics and Proteomics”.
en
Інститут експериментальної патології, онкології і радіобіології ім. Р.Є. Кавецького НАН України
Experimental Oncology
Original contributions
Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma
Article
published earlier
institution Digital Library of Periodicals of National Academy of Sciences of Ukraine
collection DSpace DC
title Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma
spellingShingle Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma
Zhuravel, E.
Efanova, O.
Shestakova, T.
Glushko, N.
Mezhuev, O.
Soldatkina, M.
Pogrebnoy, P.V.
Original contributions
title_short Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma
title_full Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma
title_fullStr Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma
title_full_unstemmed Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma
title_sort administration of vitamin d3 improves antimetastatic efficacy of cancer vaccine therapy of lewis lung carcinoma
author Zhuravel, E.
Efanova, O.
Shestakova, T.
Glushko, N.
Mezhuev, O.
Soldatkina, M.
Pogrebnoy, P.V.
author_facet Zhuravel, E.
Efanova, O.
Shestakova, T.
Glushko, N.
Mezhuev, O.
Soldatkina, M.
Pogrebnoy, P.V.
topic Original contributions
topic_facet Original contributions
publishDate 2010
language English
container_title Experimental Oncology
publisher Інститут експериментальної патології, онкології і радіобіології ім. Р.Є. Кавецького НАН України
format Article
description Aim: To analyze antitumor efficacy of experimental cancer vaccine therapy combined with introduction of vitamin D3 (VD3) for treatment of Lewis lung carcinoma (3LL). Materials and Methods: Cancer vaccines composed from recombinant murine beta-defensin-2 (mBD-2) and 3LL cell lysate, or DNA, coding for mBD-2-Muc1 fusion construct cloned in pcDNA3+ vector, were prepared and used for intradermal vaccination. Experimental cancer vaccines introduced i. d. at therapeutic and prophylactic regimens to 3LLbearing C57Bl mice, were applied alone or in combination with VD3 (administered per os) and/or low-dose cyclophosphamide (CP, administered intraperitoneal). Efficacy of treatments was analyzed by primary tumor growth dynamics indexes and by metastasis rate in vaccinated animals. Results: As it has been shown, administration of the protein-based vaccine composed from mBD-2 and 3LL cell lysate in combination with VD3 and CP, but not in VD3 free setting, led to significant suppression of primary tumor growth (p < 0.005) and had significant antimetastatic effect. Introduction of VD3 with or without CP in the scheme of treatment with mBD-2-Muc1-DNA vaccine at therapeutic regimen has led to significant suppression of primary tumor (p < 0.05) and metastasis volumes (p < 0.005), while in the groups of animals treated with DNA-vaccine + VD3 with or without CP at prophylactic regimen, significant antimetastatic effect (p < 0.05) and elevation of average life-span (p < 0.05) have been registered. Conclusion: The results of this pilot study have shown promising clinical effects of VD3 administration in combination with cancer vaccinotherapy in vivo.
issn 1812-9269
url https://nasplib.isofts.kiev.ua/handle/123456789/138597
citation_txt Administration of vitamin D3 improves antimetastatic efficacy of cancer vaccine therapy of Lewis lung carcinoma / E. Zhuravel, O. Efanova, T. Shestakova, N. Glushko, O. Mezhuev, M. Soldatkina, P.V. Pogrebnoy // Experimental Oncology. — 2010. — Т. 32, № 1. — С. 33-39. — Бібліогр.: 37 назв. — англ.
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fulltext Experimental Oncology 32, 33–39, 2010 (March) 33 Immunotherapy with the use of rationally designed cancer vaccines is presently considered as a promising approach for cancer treatment directed on enhancement of immune response against specific antigens expressed in tumor cells. As a rule, tumor antigens are poorly immu- nogenic, that’s why vaccination with tumor-associated antigens (TAAs) only doesn’t lead to induction of effective antitumor immunity. For generation of effective antitumor response it is considered reasonable to enhance it via introduction of specific chemokine molecules used in vaccine formulation as TAA carriers to antigen-presenting cells [1–3]. In the last years, along with a number of che- mokines (CCL7, CCL20, CXCL10 etc.), an antimicrobial peptide murine beta-defensin-2 (mBD-2), a molecule which ability to bind CCR6 on iDCs [4], has been used in experimental cancer immunotherapy as the carrier of genetically fused TAA, what improved significantly the clinical efficacy of the vaccinations [5–7]. In the pres- ent research devoted to experimental cancer vaccine therapy, taking into account the data of immunologic studies [5–7], we have chosen mBD-2 as a chemokine in the content of cancer vaccines; from the other side we wish to explore whether activation of in vivo expression of this peptide antibiotic may be beneficial for clinical effect of cancer immunotherapy. mBD-2 belongs to the family of small (2–6 kD) cationic microbicidal peptides that are produced by epithelial cells in response to bacterial products and proinflammatory cytokines, possess multiple biologic activities, in particular immunomodulatory ones, and compose an important chain of innate immunity sys- tem [8, 9]. Moreover, similarly to other mammalian defensins [10–12], mBD-2 may be involved in tumori- genesis playing a complex and poorly understood yet role in cancer cells and tumor microenvironment. Ac- cording to our recent results [12], mBD-2 expressed in murine Lewis lung carcinoma (3LL) cells, may pos- sibly be involved in regulation of 3LL cell proliferation in vitro and in vivo playing antiproliferative role in this experimental tumor. Down-regulation of mBD-2 mRNA expression in 3LL cells in vivo led to accelerated tumor growth and more aggressive metastasis [12]. There- fore, we hypothesized that up-regulation of mBD- 2 expression in epithelial tissues of 3LL-bearing mice in addition to immunotherapy could improve total an- ticancer effect of the treatment. In this regard we have decided to analyze whether it is possible to activate mBD-2 mRNA expression in vivo by introduction of vi- tamin D3 (VD3) to experimental animals. According to the literature data, some human antimicrobial peptides (cathelicidin [13] and human beta-defensin-2 [14]) are positively regulated by 1.25(OH)2D3 — metabolic form of VD3. The study [15] performed on mice has shown that mBD-2, mBD3 and cathelin-related antimicrobial peptide are up-regulated in mouse skin exposed to low-dose UV irradiation, and this process is mediated by cutaneous VD3 activation. To our knowledge, despite wide interest to VD3 as potent pleiotropic immunomodulating agent that may be used alone or in combination with chemothera py [16] significantly improving anticancer effect of treat- ment, there are just few publications in the field on its combined use in a setting of cancer immunotherapy. For example, in the work [17], the research has been ADMINISTRATION OF VITAMIN D3 IMPROVES ANTIMETASTATIC EFFICACY OF CANCER VACCINE THERAPY OF LEWIS LUNG CARCINOMA E. Zhuravel, O. Efanova, T. Shestakova, N. Glushko, O. Mezhuev, M. Soldatkina, P. Pogrebnoy* R.E. Kavetsky Institute of Experimental Pathology, Oncology and Radiobiology, NAS of Ukraine, Kyiv, Ukraine Aim: To analyze antitumor efficacy of experimental cancer vaccine therapy combined with introduction of vitamin D3 (VD3) for treat- ment of Lewis lung carcinoma (3LL). Materials and Methods: Cancer vaccines composed from recombinant murine beta-defensin-2 (mBD-2) and 3LL cell lysate, or DNA, coding for mBD-2-Muc1 fusion construct cloned in pcDNA3+ vector, were prepared and used for intradermal vaccination. Experimental cancer vaccines introduced i. d. at therapeutic and prophylactic regimens to 3LL- bearing C57Bl mice, were applied alone or in combination with VD3 (administered per os) and/or low-dose cyclophosphamide (CP, administered intraperitoneal). Efficacy of treatments was analyzed by primary tumor growth dynamics indexes and by metastasis rate in vaccinated animals. Results: As it has been shown, administration of the protein-based vaccine composed from mBD-2 and 3LL cell lysate in combination with VD3 and CP, but not in VD3 free setting, led to significant suppression of primary tumor growth (p < 0.005) and had significant antimetastatic effect. Introduction of VD3 with or without CP in the scheme of treatment with mBD- 2-Muc1-DNA vaccine at therapeutic regimen has led to significant suppression of primary tumor (p < 0.05) and metastasis volumes (p < 0.005), while in the groups of animals treated with DNA-vaccine + VD3 with or without CP at prophylactic regimen, significant antimetastatic effect (p < 0.05) and elevation of average life-span (p < 0.05) have been registered. Conclusion: The results of this pilot study have shown promising clinical effects of VD3 administration in combination with cancer vaccinotherapy in vivo. Key Words: experimental cancer vaccine, murine beta-defensin-2, mucin-1, Lewis lung carcinoma, vitamin D3, cyclophosphamide. Received: February 4, 2010. *Correspondence: E-mail: pogrebnoy@onconet.kiev.ua Abbreviations used: 3LL — Lewis lung carcinoma; СР — cyclophos- phamide; DC — dendritic cell; mBD-2 — murine beta-defensin-2; Muc1 — murine mucin-1; TAA — tumor-associated antigen; VD3 — vitamin D3. Exp Oncol 2010 32, 1, 33–39 34 Experimental Oncology 32, 33–39, 2010 (March) performed on 3LL model, where the efficacy of applied immunotherapy (adoptively transferred tumor-reactive lymph node cells) has been shown to be significantly elevated by introduction of VD3; the authors have registered the significant antimetastatic effect of such treatment. In a series of works [18–20] it has been demonstrated that VD3/calcitriol may be considered an effective mucosal adjuvant agent potently promot- ing immune responses to cutaneously administered vaccines. So, the first task of our work was to study the ex- pression patterns of mBD-2 mRNA in lung tissue of healthy mice treated with VD3, and the second one was to prepare anticancer protein-based and DNA- based vaccines and analyze whether their efficacy in vivo in 3LL tumor model may be increased by an introduction of VD3. MATERIALS AND METHODS Cell lines and bacterial strains. In vitro culture of transplantable 3LL cells was obtained from the Bank of Cell Lines from Human and Animal Tissues of R.E. Ka- vetsky Institute of Experimental Pathology, Oncology and Radiobiology, NAS of Ukraine (Kyiv, Ukraine). The cells were cultivated in vitro in DMEM culture medium with high glucose content supplemented with 10% fetal bovine serum, 100 units/mL penicillin, 100 μg/mL streptomycin sulfate, and 0.25 μg/mL amphotericin B as fungizone in 5% CO2 athmosphere at 37 °C. Cultivation of bacterial cells (strain E. coli DH5α) was carried out on LB medium at 37 °C. Selection and storage of recombinant colonies was performed on agarized LB medium supplemented with 50 μg/mL ampicilline or kanamycine. Gene cloning and plasmid construction. The pcDNA3-Igk-mBD-2 expression plasmid contai- ning secretable mBD-2 was created by the following way. Mouse Igk signal sequence was cloned from plasmid pSecTag2a to pcDNA3.1.+. Gene for ma- ture mBD2 was obtained from lipopolysaccharide (10 ng/ml)-treated murine BALB/c macrophages by RT-PCR using the following primers: mBD-2-F: 5’-ACCTAAGCTTCGAACTTGACCACTGCCACACC-3’ and mBD-2-R: 5’-GCCGAATTCTCATTTCATGTACTT- GCAACAGGG-3. The mature mBD2 cDNA was cloned in frame with Igk signal sequence. For construction of pcDNA3-Igk-mBD-2-Muc1, ex- tracellular domain of Muc1 fragment containing 11 tan- dem repeats was cloned by RT-PCR from total RNA of 3LL cells with the use of the following PCR pri mers: Muc1-F: 5’-GCCGAATTCACCAGCAGTTCCTTAG- CATC-3’; Muc1-R: 5’-CTACTCGAGTCATGCAGAGCT- GGTAGTTGTGAC-3’; and for mBD-2 fragment: mBD-2-F and CmBD-R: 5’-GGCGAATTCAAGATCG- GCTTTCATGTACTTGCAACAGGG-3’. The N-terminus of Muc1 was fused in frame with mBD-2 through the linker sequence. The Muc1 fragment for the control vector pcDNA3-Igk-Muc1 was amplified using the following primers pair: CMuc1-F: 5’-AACAAGCTTCAC- CAGCAGTTCCTTAGCATC -3’; Muc1-R. All constructs were verified by DNA dideoxyse- quencing method using T7 and BGH primers and puri- fied using plasmid purification kit Quiagen EndoFree (USA). Content of LPS in plasmid preparation and pro- tein-based vaccine was evaluated by standard LAL-test. Control transfection of human embryonal kidney (HEK293) cells was performed with the use of FuGene 6 reagent (Roche Molecular Biochemicals, USA) ac- cording to the instructions of the manufacturer. RT-PCR analysis. Total RNA was isolated from tis- sue samples by the method of Chromzynski and Sacchi [21]. For detection of mBD-2 or Muc1 RNA expression, semiquantitative RT-PCR analysis was performed with the use of specific primers. The expression level of beta-actin as the house-keeping gene served as a control. The relative expression level was analyzed with the use of TotalLab Program. Preparation of protein-based vaccine. For the preparation of protein-based vaccine, active recombi- nant mBD-2 produced in bacterial cells as GST-fusion protein [12], that was additionally purified from endo- toxin contaminants has been used. 3LL cell lysate was prepared from in vitro cultured 3LL cells by standard lysis of the cells with modified SDS-free RIPA buffer, and stored at –70 °C until use. In vivo study. For in vivo research, male C57Bl mice 2 months old bred in the animal facility of R.E. Ka- vetsky Institute of Experimental Pathology, Oncology and Radiobiology, NAS of Ukraine (Kyiv, Ukraine) were used. All animal procedures were carried out accor- ding to the rules of local Ethic Committee and were approved by the Ethic Board of IEPOR NASU. 3LL cells (5 x 104 cells/100 μl PBS per animal) were transplanted i.m. in right hind leg of C57Bl mice. Tu- mor growth dynamics was monitored each 5 days by means of calipers starting from day 17 after tumor cell transplantation when tumors became palpable, and till the end of experiment. At 34-th day after tumor cell transplantation, the animals were sacrificed by ether narcosis, primary tumors and lungs were removed and weighted, lung metastases were calculated, and blood serum was collected. Immunotherapy of experimental murine tumors with the use of cancer DNA vaccine or protein-based vaccine was performed at therapeutic and prophy- lactic regimens by similar schedules. In therapeutic setting, vaccine was introduced i.d. at days 2, 6, 10, and 20 after tumor cell transplantation [5]; in prophy- lactic one — at days 0, 4, 8, 18; in 2 weeks after the last immunization, 3LL cells were transplanted. For i.d. administration of DNA vaccine, the first three im- munizations (20 μg DNA/10 μL PBS) were performed with the use of tattoo device in the skin of left hind leg by the method described in [22], while the fourth vac- cination (20 μg DNA/10 μL PBS) was done i. d. in the ear of animals. In the case of protein-based cancer vaccine, it was injected i. d. only in the ear of animals (recombinant mBD-2 peptide (2 g/10 l PBS) and 3LL cell lysate (20 g/20 l PBS)). Experimental Oncology 32, 33–39, 2010 (March) 35 VD3 (10 IU/day/animal) was administered with drinking water. Cyclophosphamide (СР, 2.5 mg/100 μL PBS/animal) was administered i. p. at the days 1, 9, 19 after tumor cell transplantation as described in [23]. Experimental animals were housed in 10 groups per each protein-based vaccination setting (А — thera- peutic regimen, B — prophylactic regimen; n = 5 per group) and received the following treatment: А1 (B1) — control; А2 — mBD-2; А3 — 3LL cell lysate; А4 — 3LL + VD3; A5 — 3LL + D3 + CP; A6 — mBD-2 + 3LL; А7 — VD3; А8 — СР; А9 — mBD-2 + 3LL + VD3; А10 — mBD-2 + 3LL + VD3 + СР. Similarly, for DNA-vaccination there were 10 groups for therapy (C) and 10 groups for prophylaxis (D) (n = 5 per group) that received complete or incom- plete plasmid constructs: C1 (D1) — control (blank vector); C2 (D2) — pcDNA3-Igk-mBD-2; C3 (D3) –pcDNA3-Igk-Muc1; C4 (D4) — pcDNA3-Igk-Muc1 + VD3; C5 (D5) — pcDNA3-Igk-Muc1 + VD3 +CP; C6 (D6) — pcDNA3-Igk-mBD-2-Muc1; C7 (D7) — VD3; C8 (D8) — CP; C9 (D9) — pcDNA3-Igk-Muc1 + VD3; C10 (D10) — pcDNA3-Igk-mBD-2-Muc1 + VD3 + СР. Antitumor and antimetastatic effects of vaccina- tion were evaluated by suppression of primary tumor growth and the number of lung metastases. Each experiment was repeated twice. Statistical analysis. The data were reported as the mean  SD. The statistical significance of the differen ces between mean values was assessed by the Student’s t-test. Values p < 0.05 were considered statistically significant. Differences in survival between the groups were determined by nonparametric log-rank test. RESULTS AND DISCUSSION VD3 treatment up-regulates mBD-2 mRNA expression in murine lung tissue. Prior to vaccina- tions, we have performed an in vivo study in order to analyze whether it is possible to activate mBD-2 mRNA expression in vivo in epithelial lung cells of healthy mice by introduction of VD3. Experiment has been carried out on healthy C57Bl male mice (n = 3 per group) that received VD3 (10 IU per animal per day) per os for 10 days, or did not receive the vitamin. Then the animals were sacrificed, and mBD-2 mRNA expression level in healthy lung tissues of the animals was ana- lyzed with the use of semiquantitative RT-PCR analysis. Our data have demonstrated (Fig. 1) that consumption of VD3 resulted in up-regulation of mBD-2 expression in healthy lungs of C57Bl mice compared to the con- trol. So, we have expected that introduction of VD3 in immunotherapy schedule may lead to up-regulation of mBD-2 expression in lung tissues of experimental animals and, respectively, to elevation of its local an- tiproliferative activity [12] what may possibly improve the results of experimental immunotherapy. 0 0.05 0.1 0.15 0.2 0.25 0.3 0.35 0.4 0.45 K VD3 Re la tiv e le ve l o f m BD -2 e xp re ss io n 1 2 3 4 β-actin 284 bp mBD-2 120 bp a b Fig. 1. RT-PCR analysis of mBD-2 mRNA expression in lung tissue of healthy mice (a): mBD-2 mRNA expression in lungs of healthy animals that were treated with VD3 (line 4) vs that in control animals (line 3). Graphical representation of mBD2 mRNA expression level normalized by beta-actin expression (b) Design of experiment and selection of tumor model. For performance of vaccinations, we have used 3LL, an experimental model of murine solid tumor with high level metastasis in lungs. Transplantation of just 5 x 104 3LL cells/animal results in 100% lethality in 5 weeks period. In a setting of protein-based vaccine, we have used 3LL cell lysate as total tumor antigen. In a setting of DNA-based vaccine, to select a protein target in 3LL cells, we have performed an analysis of literature data in the field, and decided to introduce murine mucin-1 (Muc1) coding sequence in DNA vaccine. Muc1 is a highly glycosylated 200 kDa membrane protein [24], a non-polymorphic homo- log of human polymorphic epithelial mucin MUC1. The human MUC1 is expressed by a wide variety of epithelial tissues where the protein plays the important physiologic and antiinflammatory roles at normal state [25, 26]. In human epithelial cancers, MUC1 is often overexpressed, underglycosylated and lost polarized type of expression, that’s why it is recognized as uni- versal tumor antigen of human carcinoma. There are numerous experimental researches of cancer vaccines directed against MUC1 performed on MUC1-transgenic animals, and clinical trials of cancer vaccines directed against MUC1 [27, 28]; and their results are promising. In contrary, little is known about expression patterns of Muc1 in murine tumors, and experimental vaccinations with the use of wtMuc1 have been done rarely. Accor- ding to the data of literature [29], earlier with the use of experimental breast cancer model there were per- formed immunizations in C3H/HeOuj mice with mouse mucin-1 fusion protein, and in a case of combination of such immunotherapy with CP treatment antitumor effect has been registered. As far as we did not found the data on Muc1 expression patterns in murine tumor cells and in particular, in 3LL cells, we have performed semiquantitative RT-PCR analysis of Muc1 mRNA expression in 3LL-derived tumors, healthy lungs and 36 Experimental Oncology 32, 33–39, 2010 (March) heavily metastasized lungs of 3LL-bearing mice. We have registered high expression levels of Muc1 mRNA both in 3LL derived tumors, metastatic lesions, and in healthy lung cells of C57Bl mice (Fig. 2); so, being certain that Muc1 is expressed in 3LL cells, we have supposed to direct our vaccine against Muc1 in this particular tumor model despite the understandable risk of its low specificity and autoimmunity. 0 0.05 0.1 0.15 0.2 0.25 0.3 1 2 3 4 Re la tiv e le ve l o f M uc 1 ex pr es si on 1 2 3 4 β-actin 284 bp Muc1 750 bp a b Fig. 2. RT-PCR analysis of Muc1 mRNA expression in largely metastasized murine lung tissue (line 4), healthy lung tissue (lines 1, 2) and primary 3LL tumor sample (line 3). Expression of beta-actin served as a control (a). Graphical representation of mBD2 mRNA expression level normalized by beta-actin ex- pression (b) At last, according to literature data [23, 30], cancer immunotherapy efficacy could be elevated by its com- bination with low-dose chemotherapy for inhibition of immunosuppressive cancer network. That’s why we have supplemented the vaccination schedule with low-dose CP therapy (100 mg/kg). Vaccination of 3LL-bearing mice with cancer vaccine composed from recombinant mBD-2 pep- tide and 3LL cell lysate. To analyze antitumor effect of vaccination with the use of cancer vaccine com- posed from recombinant mBD-2 peptide (2 g/10 l PBS) and 3LL cell lysate (20 g/20 l PBS), we have applied both therapeutic and prophylactic administra- tion of the vaccine and its separate components with or without VD3 and CP therapy by the schemes described in Materials and Methods section. The results of therapeutic vaccination have shown (Fig. 3, 4) that administration of mBD-2 peptide to- gether with 3LL cell lysate led to statistically insignifi- cant suppression of primary tumor growth and meta- static levels in 3LL-bearing mice compared with control groups. However, introduction of VD3 into treatment schedule, especially in combination with CP therapy at metronomic regimen, has notably affected an efficacy of such vaccination and resulted in significant decrease of primary tumor volumes (group A10, p < 0.005, see Fig. 3) and the number of lung metastases (see Fig. 4). Interestingly, similar antimetastatic effect of VD3 ad- ministration has been observed in a control group of animals treated with 3LL cell lysate + VD3 (see Fig. 4) but not in the case of separate VD3 or 3LL cell lysate administration, and there were insignificant differences in lung metastasis numbers bet ween 3LL + VD3 and mBD-2 + 3LL + VD3 treated groups. Administration of CP only didn’t influence significantly primary tumor volumes, but had significant antimetastatic effect (group A8). Upon prophylactic administration of the vaccine, also the highest antimetastatic effect has been observed in the case of administration of the vaccine si- multaneously with VD3 consumption (mean lung weight in vaccine + VD3 treated animals was 190 ± 15 mg vs 295 ± 145 mg in control groups). Both prophylactic and therapeutic vaccinations had statistically insignificant influence on average life span of tumor-bearing mice (Fig. 5). 0 1 2 3 4 5 6 7 8 A1 A2 A3 A4 A5 A6 A7 A8 A9 A10 Tu m or w ei gh t, r.u . * Fig. 3. Comparative analysis of primary tumor weight (rel. units) in experimental animals from groups A1–A10 treated with pro- tein-based vaccine at therapeutic regimen at the day 34 after 3LL transplantation: А1 — control; А2 — mBD-2; А3 — 3LL cell lysate; А4 — 3LL + VD3; A5 — 3LL + D3 + CP; A6 — mBD-2 + 3LL; А7 — VD3; А8 — СР; А9 — mBD-2 + 3LL + VD3; А10 — mBD-2 + 3LL + VD3 + СР. Each group was composed from 5 animals, experi- ment was twice repeated. *Difference is significant (p < 0.005) compared to group A1. 0 0.1 0.2 0.3 0.4 0.5 0.6 A1 A2 A3 A4 A5 A6 A7 A8 A9 A10 Lu ng w ei gh t Fig. 4. Lung weight of experimental animals from groups A1– A10 treated with protein-based vaccine at therapeutic regimen at the day 34 after 3LL transplantation. Treatment groups: А1 — control; А2 — mBD-2; А3 — 3LL cell lysate; А4 — 3LL + VD3; A5 — 3LL + D3 + CP; A6 — mBD-2 + 3LL; А7 — VD3; А8 — СР; А9 — mBD-2 + 3LL + VD3; А10 — mBD-2 + 3LL + VD3 + СР. Each group was composed from 5 animals, experiment was twice repeated So, from the data of mentioned above experiments we have figure out two main conclusions. Firstly, an anticancer efficacy of protein [mBD-2 + 3LL lysate] vaccination is moderate enough and did not generate significant therapeutic and protective immunity in 3LL model. Such results could be explained by the data of investigation [4] where the authors have shown that Experimental Oncology 32, 33–39, 2010 (March) 37 effective vaccinations using beta-defensin-2 require an existence of physical link between peptide and TAA to elicit antitumor immunity. Possibly, an absence of chemical coupling between recombinant mBD-2 pep- tide and TAAs in 3LL cell lysate may explain mode rately good results of vaccination of 3LL bearing mice. Sec- ondly, our results have demonstrated that introduction of VD3 into the scheme of cancer immunotherapy may be considered reasonable and, without being toxic, notably elevates antimetastatic effect of vaccination, even in its defensin-free setting (see Fig. 4). Besides, the use of VD3 alone also led to some decrease of secondary tumors volumes, however such rates were statistically insignificant; it couldn’t be excluded that mentioned effect may be in part realized via up-regu- lation of mBD-2 gene in murine epithelial tissues. Both mentioned conclusions we have taken into account in the second part of our research directed on generation of mBD-2-containing cancer DNA vaccine. 0 10 20 30 40 50 60 0 10 20 30 40 50 60 70 80 90 100 A1 A2 A3 A4 A5 A6 A7 A8 A9 A10 Days Su rv iva l, % 0 10 20 30 40 50 0 10 20 30 40 50 60 70 80 90 100 B1 B2 B3 B4 B5 B6 B7 B8 B9 B10 Days Su rv iva l, % a b Fig. 5. Survival of 3LL-bearing mice treated with protein-based vaccine at therapeutic (a) and prophylactic (b) regimens. Each group of animals was composed from 10 animals. Log-rank test. Treatment groups: А1 (B1) — control; А2 (B2) — mBD-2; А3 (B3) — 3LL cell lysate; А4 (B4) — 3LL + VD3; A5 (B5) — 3LL + D3 + CP; A6 (B6) — mBD-2 + 3LL; А7 (B7) — VD3; А8 (B8) — СР; А9 (B9) — mBD-2 + 3LL + VD3; А10 (B10) — mBD-2 + 3LL + VD3 + СР. *Difference is significant (p < 0.05) compared to the control groups treated with blank vector. Construction of cancer DNA vaccine composed from mBD-2 and murine Muc1. To generate cancer DNA vaccine composed from mBD-2 and murine Muc1, we have constructed DNA vector — chimeric molecule containing the coding sequences of mature mBD-2 and murine Muc1 genes by the procedure described in Materials and Methods section. The constructs were tested by control transfec- tion of human embryonal kidney HEK293 cells, with the next RT-PCR analysis of Muc1 mRNA expres- sion (Fig. 6). RT-PCR analysis has demonstrated that transfection was effective, and the transfected HEK293 cells express Muc1 mRNA (see Fig. 6). 1 2 3 4 5 6 β-actin 284 bp Muc1 750 bp Fig. 6. RT-PCR analysis of Muc1 mRNA expression in control HEK 293 cells (4) and transfected НЕК-pcDNA3-Igk-Muc1 (5) and НЕК-pcDNA3-Igk-mBD-2-Muc1 cells (6). Lines 1–3 — expres- sion of beta-actin gene in HEK 293, НЕК-pcDNA3Igk-Muc1 and НЕК-pcDNA3Igk-mBD-2-Muc1 cells served as a control So, in following research we have used the next panel of vector constructs: pcDNA3.1+, pcDNA3-Igk-mBD-2, pcDNA3-Igk-Muc1, pcDNA3-Igk-mBD-2-Muc1. Evaluation of anticancer efficacy of mBD-2- Muc1-cancer DNA vaccine. To evaluate anticancer efficacy of the developed mBD-2-Muc1-DNA vaccine, we have apply vaccination protocol consisting from four sequential intradermal immunizations (20 μg DNA/10 μl PBS per animal) — first three with the use of tattoo device in skin of animal’s leg, and the forth one — i. d. in ears of mice, at therapeutic (series C) and prophylactic (series D) regimens, as described in Materials & Methods section. As it has been mentioned above, transplantation of 5 x 104 3LL cells/animal results in 100% mortality in 5 weeks period; as we have found out, vaccination with the use of DNA vaccine + VD3 + CP led to genera- tion of tumor protection in 20% of mice that received immunotherapy at prophylactic and therapeutic regimens. In the rest of animals that developed the tumors, therapeutic vaccination suppressed signifi- cantly primary tumors growth (p < 0.05) (Fig. 7) and led to significant reduction of metastasis (p < 0.005) in animals treated with vaccine + VD3 and with/without CP (Fig. 8). Prophylactic vaccination led to statistically insignificant suppression of primary tumor growth in animals treated with vaccine + VD3 + CP and significant decrease of metastasis rate in groups D4, D9, D10 (see Fig. 8); in groups C9, C10, D9 and D10 (pcDNA3- Igk-mBD-2-Muc1 + VD3 with or without CP) we have registered also the significant increase of average life-span of tumor-bearing animals (p < 0.05, Fig. 9). In conclusion, the data of in vivo experiments evi- dence on positive clinical effect of VD3 introduction into scheme of mBD-2-Muc1-DNA-based vaccination combined with low-dose CP treatment, reflected in sig- nificant antimetastatic effect and increase of average life-span of tumor-bearing animals. To be explained, the aforementioned results, without a doubt, require immunological studies, and we’ll perform them in our further research. According to recent knowledge, VD3 is a pleiotropic potent regulator of mammalian immune system [30]. Its ability to suppress autoimmune reacti vity is dem- onstrated in experimental models of type 1 diabetes, systemic lupus erythematosus, inflammatory bowel disease, autoimmune thyroiditis etc. [31, 32]. Along with immunosuppressive activity, paradoxically, VD3 has a 38 Experimental Oncology 32, 33–39, 2010 (March) positive effect as well on the system of innate immunity enhancing its response against inva ding microorgan- isms; VD3 deficiency is believed to be associated with susceptibility to some infectious diseases, in particular, tuberculosis [33]. In the last case, some possible mecha- nisms of innate defense against Mycobacterium tuber- culosis are supposed to be realized via VD3-dependent up-regulation of cathelicidin in host macrophages [34]. We believe that in present research the favoring effect of VD3 on antimetastatic efficacy of experimental cancer vaccines possibly may be in some part mediated by VD3-dependent up-regulation of mBD-2 in lung epithelial cells. Meanwhile, recent publications have shown that antitumor activity of VD3 and 1.25(OH)2D3 in vivo, due to multiple target genes of the vitamin, could be reali- zed by many ways including induction of cancer cell apoptosis, regulation of the cell cycle, up-regulation of VD3-receptor (VDR) playing a role in p53-mediated suppression of tumor growth, or regulation of a balance between proangiogenic and antiangiogenic factors thus influencing tumor angiogenesis [35–37]. Further studies in this field will help us understand the mechanisms of immunomodulatory effects of VD3 as potentially effec- tive adjuvant in cancer immunotherapy, and of its direct antitumor action. 0 1 2 3 4 5 6 7 C1 C2 C3 C4 C5 C6 C7 C8 C9 C10 Tu m or w ei gh t, r.u . 0 0.05 0.1 0.15 0.2 0.25 0.3 0.35 0.4 0.45 0.5 C1 C2 C3 C4 C5 C6 C7 C8 C9 C10 Lu ng w ei gh t, r.u . a b * * * * * Fig. 7. Primary tumors volume (a) and lung weight (b) in 3LL-bearing mice, treated with DNA vaccine at therapeutic regi- men at the day 34 after 3LL transplantation: C1 — control (blank vector); C2 — pcDNA3-Igk-mBD-2; C3 — pcDNA3-Igk-Muc1; C4 — pcDNA3-Igk-Muc1 + VD3; C5 — pcDNA3-Igk-Muc1 + VD3 +CP; C6 — pcDNA3-Igk-mBD-2-Muc1; C7 — VD3; C8 — CP; C9 — pcDNA3-Igk-mBD-2-Muc1 + VD3; C10 — pcDNA3- Igk-mBD-2-Muc1 + VD3 + СР. a — *Difference is significant (p < 0.05) compared to group C1. b — *Difference is significant (p < 0.005) compared to group C1. Each group of animals was composed from 5 animals, experiment was twice repeated. 0 1 2 3 4 5 6 D1 D2 D3 D4 D5 D6 D7 D8 D9 D10 Tu m or w ei gh t, r.u . 0 0.1 0.2 0.3 0.4 0.5 0.6 D1 D2 D3 D4 D5 D6 D7 D8 D9 D10 Lu ng w ei gh t, r.u . a b *** Fig. 8. Primary tumor volume (a) and lung weight (b) in 3LL- bearing mice, treated at prophylactic regimen with DNA vaccine at the day 34 after 3LL transplantation: D1 — control (blank vec- tor); D2 — pcDNA3-Igk-mBD-2; D3 — pcDNA3-Igk-Muc1; D4 — pcDNA3-Igk-Muc1 + VD3; D5 — pcDNA3-Igk-Muc1 + VD3 + CP; D6 — pcDNA3-Igk-mBD-2-Muc1; D7 — VD3; D8 — CP; D9 — pcDNA3-Igk-mBD-2-Muc1 + VD3; D10 — pcDNA3-Igk- mBD-2-Muc1 + VD3 + СР. *Difference is significant (p < 0.05) compared to group D1. Each group of animals was composed from 5 animals, experiment was twice repeated. 0 10 20 30 40 50 60 70 80 90 100 110 0 10 20 30 40 50 60 70 80 90 100 D1 D2 D3 D4 D5 D6 D7 D8 D9 D10 Days Days Su rv iva l, % 0 10 20 30 40 50 60 70 80 90 100 110 0 10 20 30 40 50 60 70 80 90 100 C1 C2 C3 C4 C5 C6 C7 C8 C9 C10 Su rv iva l, % a b Fig. 9. Survival of 3LL-bearing mice treated with DNA vaccine at therapeutic (a) and prophylactic (b) regimens. Each group of animals was composed from 10 animals. Log-rank test. C1 (D1) — control (blank vector); C2 (D2) — pcDNA3-Igk-mBD-2; C3 (D3) — pcDNA3-Igk-Muc1; C4 (D4) — pcDNA3-Igk-Muc1 + VD3; C5 (D5) — pcDNA3-Igk-Muc1 + VD3 + CP; C6 (D6) — pcDNA3-Igk-mBD-2-Muc1; C7 (D7) — VD3; C8 (D8) — CP; C9 (D9) — pcDNA3-Igk-mBD-2-Muc1 + VD3; C10 (D10) — pcDNA3- Igk-mBD-2-Muc1 + VD3 + СР. *Difference between groups C9 vs C1, and D9 vs D1 are significant (p < 0.05). 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